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Risdiplam is an oral drug that increases SMN protein levels by targeting the SMN2 gene manufactured…
News
In early December, Muscular Dystrophy UK and SMA UK reported our disappointment that, despite the…
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Muscular Dystrophy UK and SMA UK were extremely disappointed to learn earlier this week that,…
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Recent advances in SMA research have led to the exciting development of genetic therapies, such as…
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We are pleased to announce that the 2017 Spinal Muscular Atrophy (SMA) best practice care guide for…
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NICE widens scope of its appraisal of Zolgensma This will now be in line with the European…
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In our first condition-specific seminar, which marked SMA Awareness Month, Professor Laurent…
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On Monday 17 August, Roche announced that the European Medicines Agency (EMA) has validated the…
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The treatment, which could be the third for the condition, alongside Spinraza and Zolgensma, will…
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People with SMA Type 1 and 2 may be able to take the oral drug if Spinraza, the first treatment for…